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Rare Diseases (RD)
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Rare Diseases (RD)
Rare Diseases (RD)
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PT-018 - AI/ML DERIVED MAGNETIC RESONANCE BIOMARKERS FOR BONE FRAGILITY IN DUCHENNE MUSCULAR DYSTROPHY
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E-006 - CXCR4 ANTAGONISM CORRECTS PERIPHERAL NEUTROPENIA IN A MOUSE MODEL OF WHIM SYNDROME.
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PI-105 - EFFECT OF INDUCED HYPOGLYCEMIA ON OXIDATIVE STRESS IN HEALTHY VOLUNTEERS AND THE POTENTIAL APPLICATIONS OF N-ACETYLCYSTEINE
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PI-106 - SAFETY AND PHARMACOKINETICS OF DF-003, A TARGETED, FIRST-IN-CLASS ALPHA-KINASE 1 INHIBITOR FOR TREATMENT OF THE RARE GENETIC DISEASE, ROSAH SYNDROME.
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PII-106 - POPULATION PK AND PK/PD MODELING OF MARSTACIMAB, AN ANTI-TFPI MONOCLONAL ANTIBODY, IN ADULT AND ADOLESCENT HEMOPHILIA PATIENTS WITHOUT INHIBITORS
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OAII-001 - AI/ML DERIVED MAGNETIC RESONANCE BIOMARKERS FOR BONE FRAGILITY IN DUCHENNE MUSCULAR DYSTROPHY
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